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Perguntas e Respostas sobre a Consulta Pública | Kalydeco (ivacaftor) e  Orkambi (lumacaftor/ivacaftor) - Unidos Pela Vida
Perguntas e Respostas sobre a Consulta Pública | Kalydeco (ivacaftor) e Orkambi (lumacaftor/ivacaftor) - Unidos Pela Vida

Human epididymis protein 4 (HE4) levels inversely correlate with lung  function improvement (delta FEV1) in cystic fibrosis patients receiving  ivacaftor treatment - ScienceDirect
Human epididymis protein 4 (HE4) levels inversely correlate with lung function improvement (delta FEV1) in cystic fibrosis patients receiving ivacaftor treatment - ScienceDirect

Ivacaftor VX-770 – Cystic Fibrosis Medicine
Ivacaftor VX-770 – Cystic Fibrosis Medicine

Léčba cystické fibrózy - PROFI Medicína
Léčba cystické fibrózy - PROFI Medicína

Novel CFTR modulator combinations maximize rescue of G85E and N1303K in  rectal organoids
Novel CFTR modulator combinations maximize rescue of G85E and N1303K in rectal organoids

Burden of Illness and Pharmacoeconomic Evaluation of Lumacaftor/Ivacaftor  in Cystic Fibrosis
Burden of Illness and Pharmacoeconomic Evaluation of Lumacaftor/Ivacaftor in Cystic Fibrosis

Notiziario FFC Fondazione Ricerca Fibrosi Cistica - Onlus
Notiziario FFC Fondazione Ricerca Fibrosi Cistica - Onlus

držitel rozhodnutí o registraci
držitel rozhodnutí o registraci

PDF) Human epididymis protein 4 (HE4) levels inversely correlate with lung  function improvement (delta FEV1) in cystic fibrosis patients receiving  ivacaftor treatment
PDF) Human epididymis protein 4 (HE4) levels inversely correlate with lung function improvement (delta FEV1) in cystic fibrosis patients receiving ivacaftor treatment

Cystic Fibrosis Centre
Cystic Fibrosis Centre

O acesso aos moduladores para fibrose cística: que esperança temos e o que  podemos fazer? - Unidos Pela Vida
O acesso aos moduladores para fibrose cística: que esperança temos e o que podemos fazer? - Unidos Pela Vida

Maquetación 1
Maquetación 1

Frontiers | Organoid Technology: A Reliable Developmental Biology Tool for  Organ-Specific Nanotoxicity Evaluation
Frontiers | Organoid Technology: A Reliable Developmental Biology Tool for Organ-Specific Nanotoxicity Evaluation

LSHTM Research Online
LSHTM Research Online

Maquetación 1
Maquetación 1

Pseudomonas aeruginosa in cystic fibrosis patients with c.1652G›A  (G551D)‐CFTR treated with ivacaftor—Changes in microbiological parameters -  Millar - 2018 - Journal of Clinical Pharmacy and Therapeutics - Wiley  Online Library
Pseudomonas aeruginosa in cystic fibrosis patients with c.1652G›A (G551D)‐CFTR treated with ivacaftor—Changes in microbiological parameters - Millar - 2018 - Journal of Clinical Pharmacy and Therapeutics - Wiley Online Library

Novel CFTR modulator combinations maximize rescue of G85E and N1303K in  rectal organoids
Novel CFTR modulator combinations maximize rescue of G85E and N1303K in rectal organoids

PDF) Ivacaftor in cystic fibrosis adults: Czech experience with six years  of follow-up
PDF) Ivacaftor in cystic fibrosis adults: Czech experience with six years of follow-up

PDF) Cystic fibrosis in adults
PDF) Cystic fibrosis in adults

LSHTM Research Online
LSHTM Research Online

Novel CFTR modulator combinations maximize rescue of G85E and N1303K in  rectal organoids
Novel CFTR modulator combinations maximize rescue of G85E and N1303K in rectal organoids

Ivacaftor VX-770 – Cystic Fibrosis Medicine
Ivacaftor VX-770 – Cystic Fibrosis Medicine

Drug modulation, new drugs (section 2) – Cystic Fibrosis Medicine
Drug modulation, new drugs (section 2) – Cystic Fibrosis Medicine

Novel CFTR modulator combinations maximize rescue of G85E and N1303K in  rectal organoids
Novel CFTR modulator combinations maximize rescue of G85E and N1303K in rectal organoids